Related Conditions and Treatments
Acute Lymphoblastic Leukemia (ALL)
In the form of leukemia known as acute lymphoblastic leukemia (ALL), a group of white blood cells called lymphocytes is affected.
Adrenoleukodystrophy (ALD) is a rare genetic condition that causes the buildup of very long chain fatty acids (VLCFAs) in the brain.
Aplastic anemia occurs when the bone marrow produces too few cells.
Childhood brain tumors can be benign (non-cancerous) or malignant (cancerous), but both types can be life-threatening.
Chronic Granulomatous Disease (CGD)
Chronic granulomatous disease (CGD) is an inherited immune system disorder that occurs when a type of white blood cell does not work properly.
Chronic Myeloid Leukemia
Chronic myeloid leukemia (CML) is a form of leukemia that develops in the bone marrow, the soft, spongy center of long bones.
Congenital Amegakaryocytic Thrombocytopenia
Congenital amegakaryocytic thrombocytopenia (CAMT) is a rare, inherited disorder characterized by a severely low number of megakaryocytes.
Learn more about Congenital Amegakaryocytic Thrombocytopenia
Dyskeratosis congenita is a rare condition that can often cause bone marrow failure.
Fanconi anemia is a severe lifelong condition that requires ongoing medical treatment. Boston Children's Hospital can help.
Gene therapy is a technique used in an effort to treat or prevent disease.
Hodgkin lymphoma is a type of cancer that causes cells in the lymphatic system to abnormally reproduce.
Juvenile Myelomonocytic Leukemia
Juvenile myelomonocytic leukemia (JMML) is a rare type of blood cancer that occurs when bone marrow production of white blood cells becomes severely disregulated.
Morquio syndrome is a rare genetic condition that affects a child’s bones and spine, organs, and physical abilities.
Myelodysplastic Syndrome in Children
Myelodysplastic syndrome (MDS) is a rare disease of the blood, only occurring in four out of every 1 million children.
Neuroblastoma is a cancerous tumor that begins in nerve tissue of young children.
Non-Hodgkin lymphomas (NHLs) all start in lymph tissue and share some similarities in how the cells look under a microscope.
Pearson syndrome is a very rare condition that affects various parts of the body, and it is caused by a mutation — or changing of structure — in the mitochondrial DNA.
Pediatric Stem Cell Transplantation
A stem cell transplant (also called bone marrow transplant) is the infusion of healthy stem cells into the body to stimulate new bone marrow growth.
Severe Combined Immunodeficiency (SCID)
Severe combined immunodeficiency (SCID), often called “bubble boy disease,” is very rare, genetic disorder.
Sickle Cell Disease
Sickle cell disease is an inherited blood disorder where cells cluster together, making it difficult for them to move through small blood vessels, thus denying oxygen to the blood.
Thalassemia is an inherited blood disorder that causes the body to produce less hemoglobin than normal.
Wilms tumor is a cancerous tumor in the cells of the kidney.
Wiskott-Aldrich syndrome is a rare genetic immunodeficiency that keeps a child's immune system from functioning properly.