Summary
An Open-Label, Long-Term Follow Up Study of Safety and Efficacy in PKU Subjects with PAH Deficiency Previously Administered HMI 102
Conditions
Phenylketonuria, PAH Deficiency
Recruitment Status
ENROLLING_BY_INVITATION
Detailed Description
This Long-Term Follow Up Study will evaluate the safety and efficacy of PKU Subjects with PAH Deficiency Previously Administered HMI 102. Subjects will have already received a single dose of HMI-102 administered intravenously
Eligibility Criteria
Inclusion Criteria:
* Subject was previously administered HMI 102.
* Subject is able to understand the purpose and risks of the study and is willing to provide informed consent.
* Subject is able to comply with all study procedures and long-term follow-up.
Exclusion Criteria:
* Participation in the study is not in the subject's best interest, in the opinion of the Investigator.
Intervention
Intervention Type
Intervention Name
GENETIC
HMI-102
Gender
ALL
Min Age
18 Years
Max Age
55 Years
Download Date
2022-06-30
Principal Investigator
N/A
Primary Contact Information
For more information on this trial, visit clinicaltrials.gov.
Contact
For more information and to contact the study team: