Research at Boston Children's Hospital

The research enterprise at Boston Children’s Hospital, comprising more than 3,000 researchers, is the world’s largest at a pediatric center. Our work is fueled by a deep understanding of disease coupled with world-class discovery platforms, including genetics and genomics, gene editing, bioinformatics, proteomics, bioengineering, image analysis, multiple animal models, biobanks and disease-specific stem cell lines. We have special expertise in rare disease discovery and see large, highly diverse patient populations.

michael rogers and danielle peterse

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More than 3,000 researchers & scientific staff

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1 million square feet of research space — and growing

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$388 million in total research funding FY2018 — #1 NIH funding for pediatric research

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A new frontier: Inside a custom drug

Dr. Yu and his team of scientists pulled off something unprecedented, something seemingly impossible. In the space of 10 months, they pinpointed Mila’s rare mutation, designed a drug to bypass it, engaged industry partners and FDA regulators, and launched a treatment trial — just for Mila.

Early encouraging results are reported in The New England Journal of Medicine. They could open a new path, showing it’s possible to create personalized genetic therapies for children with rare conditions — and to do so quickly.

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Dr. Yu batten disease

Boston Children's Hospital Innovation

BCH Innovation News @BCH_Innovation 11/16/2019 7:00:00 PM
About 2 billion people suffer from deficiencies of #micronutrients. Now, researchers at @MIT may have found a way t…
BCH Innovation News @BCH_Innovation 11/16/2019 5:00:01 PM
A team of scientists from @BostonChildrens, @TechnionLive and @wrair use #WGS and #deepsequencing to find match bet…
BCH Innovation News @BCH_Innovation 11/15/2019 6:00:00 PM
Researchers hope a new technology known as "eRapid" will enable great advances in our ability to develop handheld d…
BCH Innovation News @BCH_Innovation 11/15/2019 5:00:11 PM
86% of #diet trials for #obesity in the past 10 years amended their outcome measures, raising the possibility of bi…
BCH Innovation News @BCH_Innovation 11/15/2019 4:00:01 PM
A new $1.98 million study, funded by AHRQ, will use natural #languageprocessing to supplement surveillance for…
BCH Innovation News @BCH_Innovation 11/15/2019 3:00:00 PM
#Nitazoxanide or a derivative drug could complement current tuberculosis regimens by boosting #innateimmunity, sugg…
Building on our extraordinary leadership in pediatric science at Boston Children’s, we translate our findings — and those of others — to fundamentally change how disease is treated and cured.

David A. Williams, MD
Senior Vice President and Chief Scientific Officer