 |
|
Clinical Research Previously Conducted at Children's Hospital, Completed.
|
|
4 Entries Found
|
 |
| Principal Investigator: |
Basil T. Darras
|
| Department: |
Neurology |
| Protocol Title: |
CLINICAL STUDY OF SPINAL MUSCULAR ATROPHY |
| Protocol Status: |
Recruitment Complete
|
|
Trial Description:
|
|
|
|
 |
| Principal Investigator: |
Basil T. Darras
|
| Department: |
Neurology |
| Protocol Title: |
A PILOT STUDY OF BIOMAKERS FOR SPINAL MUSCULAR ATROPHY |
| Protocol Status: |
Recruitment Complete
|
|
Trial Description:
|
|
|
|
 |
| Principal Investigator: |
Basil T. Darras
|
| Department: |
Neurology |
| Protocol Title: |
A PHASE 2B EFFICACY AND SAFETY STUDY OF PCT124 IN SUBJECTS WITH NONSENSE-MUTATION-MEDIATED DUCHENNE AND BECKER MUSCULAR DYSTROPHY |
| Protocol Status: |
Recruitment Complete
|
|
Trial Description:
|
|
|
|
 |
| Principal Investigator: |
Basil T. Darras
|
| Department: |
Neurology |
| Protocol Title: |
A PHASE I/IIA CLINICAL TRIAL OF SODIUM PHENYLBUTYRATE IN PEDIATRIC SUBJECTS WITH TYPE I SPINAL MUSCULAR ATROPHY (SMA), NPTUNE02: VERSION 3.0, OCTOBER 2, 2007 |
| Protocol Status: |
Recruitment Complete
|
|
Trial Description:
|
|
|
|