Research at Boston Children's Hospital

The research enterprise at Boston Children’s Hospital, comprising more than 3,000 researchers, is the world’s largest at a pediatric center. Our work is fueled by a deep understanding of disease coupled with world-class discovery platforms, including genetics and genomics, gene editing, bioinformatics, proteomics, bioengineering, image analysis, multiple animal models, biobanks and disease-specific stem cell lines. We have special expertise in rare disease discovery and see large, highly diverse patient populations.

michael rogers and danielle peterse

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More than 3,000 researchers & scientific staff

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1 million square feet of research space — and growing

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$388 million in total research funding FY2018 — #1 NIH funding for pediatric research

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A new frontier: Inside a custom drug

Dr. Yu and his team of scientists pulled off something unprecedented, something seemingly impossible. In the space of 10 months, they pinpointed Mila’s rare mutation, designed a drug to bypass it, engaged industry partners and FDA regulators, and launched a treatment trial — just for Mila.

Early encouraging results are reported in The New England Journal of Medicine. They could open a new path, showing it’s possible to create personalized genetic therapies for children with rare conditions — and to do so quickly.

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Dr. Yu batten disease

Boston Children's Hospital Innovation

BCH Innovation News @BCH_Innovation 10/20/2019 5:00:00 PM
Last year, @BostonChildrens Dr. Marc Ackerman founded the American Teledentistry Association, aiming to educate den…
BCH Innovation News @BCH_Innovation 10/20/2019 1:00:01 PM
.@physicianswkly reports on a new study from @BostonChildrens Laura Nuzzi that finds #breastreduction surgery impro…
BCH Innovation News @BCH_Innovation 10/19/2019 8:00:00 PM
A new study shows starting statins during childhood for kids with FH provides benefits in adulthood. Boston Childre…
BCH Innovation News @BCH_Innovation 10/19/2019 6:00:01 PM
A new study has solved the “yellow fly mystery” that's stumped researchers for decades. @physorg_com shares the fin…
BCH Innovation News @BCH_Innovation 10/19/2019 3:30:00 PM
A new study finds brain activity patterns in the first year of life may predict #autism in infants at high risk for…
BCH Innovation News @BCH_Innovation 10/16/2019 1:04:19 PM
RT @CynGaribaldi: International Simulation Leaders at Boston Children’s Hospital, Dr. Peter Weinstock with visiting professor Dr. Guoping L…
Building on our extraordinary leadership in pediatric science at Boston Children’s, we translate our findings — and those of others — to fundamentally change how disease is treated and cured.

David A. Williams, MD
Senior Vice President and Chief Scientific Officer