Our innovative approach
Our team works closely with Children's researchers who are devoted to the study of genes that underlie inherited disorders and to finding new treatments and cures.
- Clinical trials are underway to test a drug developed at Children's to treat phenylketonuria, a disorder in which the body can't break down certain proteins.
- Children's Manton Center is the world's only center studying "orphan" diseases — those affecting fewer than 200,000 people, mostly children, in the United States.
- Researchers have found several genes linked to appetite and weight, paving the way for possible ways to prevent and treat obesity.